| Product & disease | Type of therapy | Delivery | AAV serotype | Design approach | Proof of concept | IP registration | Preclinical trials | Clinical trials phase 1 | Clinical trials phase 2 | Product rights |
|---|---|---|---|---|---|---|---|---|---|---|
|
ART_THR_01
|
||||||||||
| AAV |
subretinal
injection |
AAV8 | ||||||||
|
ART_THR_02
|
||||||||||
| AAV-mediated RNA interference |
subretinal
injection |
sAAV-ART | ||||||||
|
ART_TR_03
|
||||||||||
| AAV8-CRISPR / Cas9 Nrl sgRNA construct |
subretinal
injection |
sAAV-ART | ||||||||
|
ART_THR_04
|
||||||||||
| Possible AAV therapy |
subretinal
injection |
sAAV-ART |